Uniting Leaders to Discuss Equitable Access and Innovation in Rare Disease

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ATTENDEES

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SPEAKERS

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SPONSORS AND EXHIBITORS

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RESEARCH POSTERS

Advancing Rare Disease Research and Policy with a Focus on Equity and Innovation

The NORD® Rare Diseases and Orphan Products Breakthrough Summit® convenes thought leaders from patient advocacy organizations, industry, academia, research and government to discuss the most timely and critical topics facing the rare disease community.

With a theme of “Equitable Access to Innovation”, the 2024 NORD Summit will feature thought-provoking discussions and actionable strategies on the latest advances in clinical trials, gene therapy, medical devices, AI and patient-focused drug development with an underlying focus on inclusion and equal access for all. In addition, there will be ample opportunities for networking and the opportunity to learn about the latest rare disease research in our Poster Hall.

Some of the rare disease leaders and innovators you'll hear from at the 2024 NORD Breakthrough Summit

Giacomo Chiesi

Head of Global Rare Disease and Member of the Board, Chiesi Pharmaceuticals

Brian Goff

Chief Executive Officer, Agios Pharmaceuticals

Kate Haviland

President and CEO, Blueprint Medicines

Rachid Izzar

Executive Vice President, Global Product Strategy & Commercialization, Biogen

Julie Kim

President, US Business Unit and US Country Head, Takeda

Peter Marks, MD, PhD

Director, Center for Biologics Evaluation & Research (CBER), US Food and Drug Administration (FDA)

Dominique C. Pichard, MD, MS

Director, Division of Rare Diseases Research Innovation, NIH

Mei Baker, MD, FACMG

Professor, Division of Genetics and Metabolism, University of Wisconsin School of Medicine and Public Health; Director of Newborn Screening Program, Wisconsin State Laboratory of Hygiene

2024 Sponsors

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