Uniting Leaders to Discuss Equitable Access and Innovation in Rare Disease

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ATTENDEES

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SPEAKERS

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SPONSORS AND EXHIBITORS

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RESEARCH POSTERS

Shape the future of rare disease treatments, research and policy at the NORD® Rare Diseases and Orphan Products Breakthrough Summit.® Together, we can advance equity and innovation for the more than 30 million Americans – and more than 400 million people worldwide – with rare diseases!

Join Us

Some of the rare disease leaders and innovators you'll hear from at the 2024 NORD Breakthrough Summit

Robert M. Califf, MD

Commissioner of Food and Drugs, Food and Drug Administration (FDA)

Meena Seshamani, MD, PhD

Deputy Administrator and Director, Center for Medicare, Centers for Medicare & Medicaid Services (CMS)

Giacomo Chiesi

Head of Global Rare Disease and Member of the Board, Chiesi Pharmaceuticals

Rachid Izzar

Executive Vice President, Global Product Strategy & Commercialization, Biogen

Peter Marks, MD, PhD

Director, Center for Biologics Evaluation & Research (CBER), US Food and Drug Administration (FDA)

Michelle Tarver, MD, PhD

Interim Director, Center for Devices and Radiological Health (CDRH), US Food and Drug Administration

Patrizia Cavazzoni, MD

Director, Center for Drug Evaluation & Research (CDER), U.S. Food & Drug Administration

Hilary Marston, MD, MPH

Chief Medical Officer, FDA

Why Attend?

Collaborate & Influence

Contribute to critical discussions, forge valuable partnerships, and help advance equitable access to rare disease research and
patient care.

Engage with Experts

Connect with influential voices and stakeholders shaping the future of rare disease treatments, research and policy.

Discover Innovations

Learn about cutting-edge advancements to improve access to clinical trials, and discover emerging trends and issues that are poised to redefine the landscape of rare disease.

2024 Sponsors

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