What to Expect

Calling all champions of innovation

Join over 900 patient leaders, researchers and scientists, healthcare advocates, pharma and biotech innovators, government agencies, and others to tackle the most pressing issues facing the rare disease community.

Register Today

Pharma and Biotech

  • Hear the latest in orphan product development from top FDA leaders

  • Explore new business ventures

  • Connect with patient advocates

Government Officials and Regulators

  • Understand the policy and regulatory impact on orphan products

  • Learn about scientific advancement in the rare disease community

CROS and Solutions Companies

  • Connect with clients

  • Cultivate prospects who require your expertise and services to develop pipelines, conduct trials and studies, and pursue commercialization

Patient Advocacy Leaders

  • Understand the policy and regulatory impact on orphan products

  • Learn about scientific advancement in the rare disease community

Researchers and Scientists

  • Engage with cutting-edge research and innovative solutions

  • Network with peers and explore collaboration opportunities